Vosoritide
2 articoli — 2021-2021
Argomenti correlati
Rare Diseases (44)
Growth hormone (29)
Genetic Therapy (28)
short stature (23)
Gene therapy (21)
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Terapia genica (17)
Dwarfism (16)
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bassa statura (16)
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Spinal Muscular Atrophy (SMA) (5)
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Receptor, Fibroblast Growth Factor, Type 3 (2)
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